Biostatist Logo
Biostatist
Sample Size

The Target Effect Behind Sample Size: From Clinical Rationale to Assumption

Choose a target effect using clinical importance, external evidence and sensitivity scenarios rather than automatic Cohen thresholds.

Admin
June 20, 2026
8 min read

Effect size is the most consequential sample-size input

An optimistic target underpowers the study; an unnecessarily tiny target can make it infeasible. Justify the value prospectively.

Practical framework

  • Define the primary outcome and meaningful target.

  • Use intervals from comparable populations and designs.

  • Treat small pilot estimates as uncertain.

  • Calculate optimistic, expected and conservative scenarios.

Reporting

Report the target difference, variance, standardisation and evidence source.

Common mistakes

  • Using Cohen labels without context.

  • Treating a pilot estimate as precise.

  • Selecting evidence only from significant studies.

References

Accessed 20 June 2026. General methodological information.